Published on in A Child's Sight
Diagnosed with Leber congenital amaurosis as a baby, Hannah was on a path to going blind until gene therapy at Children’s Hospital restored her sight.
Published on in CHOP News
A groundbreaking clinical trial of gene therapy for a form of congenital blindness, co-sponsored by CHOP, earned award for distinguished clinical research.
Published on in CHOP News
Gene therapy for congenital blindness has taken another step forward, as researchers further improved vision in three adult patients previously treated in one eye.
Published on in CHOP News
Researchers at The Children's Hospital of Philadelphia show that a second dose of gene therapy for inherited blindness is safe in animals.
Published on in CHOP News
The Children's Hospital of Philadelphia was lauded for significant contributions to medical science in 2009 for dispelling myths that vaccines cause autism, and developing gene therapy to treat blindness.
Published on in CHOP News
A CHOP/Penn Medicine study used gene therapy to safely improve vision in five children and seven adults with a Leber’s congenital amaurosis, a form of blindness.