Thalassemia Center Patient Stories
1 - 3 of 3
Experimental Gene Therapy for Beta Thalassemia: Aliya’s Story
![Aliya as a baby Aliya as a baby](https://www.chop.edu/sites/default/files/styles/teaser/public/experimental-gene-therapy-patient-aliya-16x9.jpg?itok=hODs7Tzn)
For the first 30 years of her life, Aliya needed monthly blood transfusions for her inherited blood disorder. A gene therapy changed everything.
Beta Thalassemia Major: Mia’s Story
![Mia and her brother John girl hospital patient and brother](https://www.chop.edu/sites/default/files/styles/teaser/public/mia-john-16x9.jpg?itok=u1On4ln7)
From the time she was just a few months old, Mia needed blood transfusions due to her rare blood disease. A bone marrow transplant changed everything.
Beta Thalassemia Major: Nicholas's Story
![Nicholas finger painting Boy hospital patient finger painting and smiling](https://www.chop.edu/sites/default/files/styles/teaser/public/Nicholas-16x9.jpg?itok=THoOGmgo)
Beta thalassemia major forced Nicholas to undergo regular blood transfusions until he received a lifesaving bone marrow transplant.