Frequently Asked Questions about Gene Therapy for Hemophilia
Explore answers to the most common questions asked about gene therapy for hemophilia.
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National Organization for Rare Disorders (NORD)
The National Organization for Rare Disorders (NORD) provides advocacy, education and other services to improve the lives of all people affected by rare diseases.
About Hemophilia
Hemophilia is a genetic disease that prevents blood from clotting properly leading to prolonged internal and external bleeding. Read more hemophilia and the existing treatments.
Gene Therapy in Hemophilia
View interactive webinars, educational resources and the latest news about hemophilia.
Cornelia de Lange Syndrome Foundation Inc.
The Cornelia de Lange Syndrome Foundation is a nonprofit organization providing families and caregivers with a wealth of support, services, education and information about Cornelia de Lange syndrome (CdLS).