The findings from the clinical trial were published in the New England Journal of Medicine.

Researchers at Children’s Hospital of Philadelphia (CHOP) and the Perelman School of Medicine at the University of Pennsylvania revealed a powerful new bone marrow atlas that will offer the public a first-of-its-kind visual passport into the spectrum of healthy and diseased blood production.

Target gene could serve as the basis of a future therapeutic intervention.

The study identified obstacles like limited time during clinical visits, a lack of comprehensive resources, and insufficient notice from caregivers to prepare for discussions.

In a landmark study, an international consortium led by researchers at CHOP published the final results of a key clinical trial of the gene therapy CASGEVY for the treatment of sickle cell disease.

Findings provide some of the first evidence of potential therapeutic targets for condition affecting thousands of patients with single ventricle congenital heart disease.

Researchers revealed new insights into the long-term effects of bronchopulmonary dysplasia (BPD), a chronic lung disease that primarily affects premature infants, on patient health.

The methodology developed in this study could help guide clinical trial design for many rare diseases

The large study also confirmed known risk factors for COVID-19 associated with asthma in children.

FOXO1 is required for memory in T cells and is associated with more durable clinical responses to CAR T cell therapy.