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Research Studies

Cancer Center Research Studies

Find research studies available to children cared for by the Cancer Center team.

Existing patients or family members
New patients, referrals and second opinions

Recruitment Status

Clinical trial phase

Beckwith-Wiedemann Syndrome (BWS) Overgrowth Registry

The primary objective of this registry/repository is to store ongoing clinical data and biospecimens to facilitate the conduct of research on disorders of growth, genetic, and epigenetic alterations. This can also include storage of samples and data from relatives of the index patients to serve as study controls.

Phase: N/A

Actively recruiting: Yes

Category: Adults, Children, Healthy Controls

Conditions: Beckwith-Wiedemann syndrome/spectrum

PTX-022 in the Treatment of Microcystic Lymphatic Malformations

The purpose of this study is to see if a new investigational topical (applied to the skin) formulation of sirolimus, PTX-022 (the study drug), is safe and effective in treating participants with microcystic Lymphatic Malformations.

Phase: Phase III

Actively recruiting: Yes

Category: Adults, Children

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