Hemophilia and Bleeding Disorders Program Patient Stories

Bill’s hemophilia caused several serious health crises. After nearly 60 years of continual treatments, a gene therapy transformed his life.

For 50-plus years, Jay dealt with the frequent treatments needed for his hemophilia. A gene therapy put an end to the treatments and to the worry the disease caused him.

For nearly 50 years, Bill needed frequent treatment for hemophilia — often every few days. A gene therapy changed everything.