Sickle Cell and Red Cell Disorders Curative Therapy Center (CuRED) News and Updates

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FDA Approves Two Gene Therapies for Sickle Cell Disease

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FDA Approves First CRISPR-Based Therapy for Sickle Cell Disease

The Food and Drug Administration (FDA) has approved CASGEVY™ (exagamglogene autotemcel) and LYFGENIA™ (lovotibeglogene autotemcel), the first two gene therapies for the treatment of sickle cell disease  in patients 12 years and older with recurrent vaso-occlusive crises (VOCs).