The US Food and Drug Administration has approved two new breakthrough therapies for patients with sickle cell disease (SCD), and we believe both may enhance the treatment of our patients here at CHOP.Read more
Sickle Cell and Red Cell Disorders Curative Therapy Center (CuRED) News and Updates
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Published on in CHOP in the Media
The US Food and Drug Administration has granted accelerated approval to two novel drugs to treat sickle cell disease.
Published on in CHOP News
Stefano Rivella, PhD, an expert in creating the next-generation lentiviral vectors for the cure of hemoglobinopathies including sickle cell disease (SCD), as well as a leader in the discovery of erythroid and iron disorders including beta-thalassemia, has led three new published studies that make significant contributions to the scientific body of literature regarding red blood cells, and how manipulating the production of red cells can lead to the development of new disease-modifying therapies.