Clinical In Vivo Gene Therapy News

Our experts are at the forefront of clinical in vivo gene therapy breakthroughs.

CHOP Researchers Develop Innovative Model Offering New Insights to Improve and Overcome Current Obstacles in Hemophilia A Gene Therapy

Sep 5, 2024

Researchers at CHOP announced the results of a new study offering insights into the development of next-generation gene therapies to treat hemophilia A.

Experts in the Hemostasis and Thrombosis Center at CHOP Provide Expert Commentary on Hemophilia

Aug 18, 2023

Leslie Raffini, MD, and Regina Butler, RN, were quoted in the Philadelphia Inquirer on a story featuring a CHOP patient family living with hemophilia, an inherited bleeding disorder that prevents blood from clotting properly.

NIH Awards Penn Medicine and Children’s Hospital of Philadelphia $26 Million Grant to Develop Therapies for Rare Newborn Genetic Diseases

Aug 1, 2023

A Penn Medicine and CHOP team will seek to develop treatments for three rare, incurable genetic diseases with the help of a $26 million grant from the National Institutes of Health.

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Clinical In Vivo Gene Therapy News

CHOP Researchers Develop Innovative Model Offering New Insights to Improve and Overcome Current Obstacles in Hemophilia A Gene Therapy

Experts in the Hemostasis and Thrombosis Center at CHOP Provide Expert Commentary on Hemophilia

NIH Awards Penn Medicine and Children’s Hospital of Philadelphia $26 Million Grant to Develop Therapies for Rare Newborn Genetic Diseases

CHOP Expert Breaks Down Latest Hemophilia A Gene Therapy Data

CHOP Will Be Provider in Independence Blue Cross’s Gene Therapy Network

Two New Treatments for Spinal Muscular Atrophy Offer Hope

‘I Can See It!’ — From Idea to Astonishing Result

CHOP Hematologist Dr. Lindsey George Receives 2019 Clinical Achievement Research Award

Children's Hospital of Philadelphia Celebrates FDA Approval of Gene Therapy for Inherited Blindness