Groundbreaking Gene Therapy Solves Lily's Sickle Cell Disease
After years of care at CHOP, including groundbreaking gene therapy delivered as part of a clinical trial, 11-year-old Lily continues to not only grow and gain but thrive.
Patient stories
Sickle Cell Disease Patient Stories
Gene Therapy for Sickle Cell Disease: Segun’s Story
An FDA-approved gene therapy eliminates acute pain episodes for people with sickle cell disease and transforms their life expectancy.
Bone Marrow Transplant for Sickle Cell Disease: Asher’s Story
For years, sickle cell disease caused frequent pain crises and hospitalizations for Asher. A curative therapy has eliminated those harrowing experiences.
Bone Marrow Transplant for Sickle Cell Disease: Dallas’ Story
Sickle cell disease brings constant fear of life-threatening complications. A successful bone marrow transplant ended those fears for Dallas and her family.