For nearly 50 years, Bill needed frequent treatment for hemophilia — often every few days. A gene therapy changed everything.

Eliza’s family brought her to CHOP for its expertise in hyperinsulinism. She became the 600th patient to have pancreas surgery and went home cured.

Amir was born with multiple spinal problems. Surgeries at CHOP have helped straighten his spine, improving his self-confidence.

Just a few days after he was born, Kylen suffered four seizures and was diagnosed with epilepsy.

In 2000, Christian had fetal surgery for spina bifida at CHOP. Today, he’s an EMT. Follow his journey.

When their foster daughter faced insurmountable odds, a Delaware couple turned to CHOP for help with complications from spinal muscular atrophy.

Debilitating pain without a known injury can strike some of the most driven and high-achieving youth. A CHOP program offers support, treatment and relief.

After learning their unborn daughter’s life was at risk from a tumor growing on her tailbone, Lyra’s parents found hope in the SCT experts at CHOP.

Call it a mother’s intuition. Though Killian appeared to be growing and developing normally during prenatal appointments, Jennifer couldn’t stop worrying something was wrong.

When a 20-week-old fetus was diagnosed with a large goiter, CHOP experts offered a novel solution – regular infusions of thyroid hormone into the umbilical cord.

Fetal surgery for severe CDH gave AJ’s lungs a chance to grow before birth, improving his chances of a better outcome. Today, the 6-year-old is thriving.

Asher came to CHOP for a fetal surgery procedure called FETO to treat his severe CDH before he was born, giving him the best chance to survive and thrive.

While Julia’s diagnosis of a brain tumor was a shock to her family, the location and type of tumor meant surgery at CHOP was the only treatment she needed.

After Molly qualified for a kidney transplant, a new organ from a living donor was identified thanks to CHOP’s involvement with the National Kidney Registry.

Counseling on its own wasn’t enough to help Effie regulate her behavior. After working with CHOP, she started on medication and now can control her emotions.

Diagnosed with celiac disease in first grade, Emma, now 9, rallies for changes in food labeling to better protect kids like her.

A family finds hope at CHOP and now advocates for continued autism acceptance, research and support.

After being diagnosed with autism, Snai began receiving various therapies. But his family’s emphasis on emotional intelligence has truly helped him thrive.

Siblings with very different manifestations of autism both find the support and resources they need through CHOP’s Center for Autism Research.

CHOP support helps Luke and Esmeralda’s family access vital resources. The family is grateful to have such a positive community.