Blood and Marrow Transplant Program Patient Stories
1 - 10 of 21
X-linked Lymphoproliferative Disease 1: Rafi’s Story

Genetic sequencing revealed that Rafi had an extremely rare, often fatal disease — and the discovery was amazingly made before he had serious symptoms.
Bone Marrow Transplant for Sickle Cell Disease: Asher’s Story

For years, sickle cell disease caused frequent pain crises and hospitalizations for Asher. A curative therapy has eliminated those harrowing experiences.
Bone Marrow Transplant for Sickle Cell Disease: Dallas’ Story

Sickle cell disease brings constant fear of life-threatening complications. A successful bone marrow transplant ended those fears for Dallas and her family.
Bone Marrow Transplant to Treat Hurler Syndrome: Josie’s Story

18-month-old Josie received a stem cell transplant to stop a rare and devastating genetic condition in its tracks.
Bone Marrow Transplant for Hurler Syndrome: Ethan’s Story

Diagnosed before his first birthday with a rare disease that causes ongoing damage to cells and organs, Ethan quickly received the only treatment that prevents further disease.
Beta Thalassemia Major: Mia’s Story

From the time she was just a few months old, Mia needed blood transfusions due to her rare blood disease. A bone marrow transplant changed everything.
Endocrine Late Effects After Cancer Treatment: Raine’s Story

Treatment for childhood leukemia has had several long-term effects on Raine’s health, but this successful college graduate is pursuing her dream.
Beta Thalassemia Major: Nicholas's Story

Beta thalassemia major forced Nicholas to undergo regular blood transfusions until he received a lifesaving bone marrow transplant.
Medulloblastoma and Kawasaki Disease: Gabby’s Story

"CHOP is so great because they support the whole family," says Gabby's dad, Paul.
Severe Congenital Neutropenia: Emma’s Story

Emma’s bone marrow wasn’t producing what her body needed to fight infections. A bone marrow transplant transformed her life.