Blood and Marrow Transplant Program Patients Stories Listing

Every person on your child’s team has the same goal: to give your child the best possible care. Our highly skilled team includes medical experts in each step of the transplant process. We also offer nutrition counseling, emotional support, financial counseling and more.

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215-590-2280

Patient story

Gene Therapy for Sickle Cell Disease: Marie-Chantal’s Story

An FDA-approved gene therapy is giving people with sickle cell disease a future they didn’t think they’d have.

Patient story

X-linked Lymphoproliferative Disease 1: Rafi’s Story

Genetic sequencing revealed that Rafi had an extremely rare, often fatal disease — and the discovery was amazingly made before he had serious symptoms.

Patient story

Bone Marrow Transplant for Sickle Cell Disease: Asher’s Story

For years, sickle cell disease caused frequent pain crises and hospitalizations for Asher. A curative therapy has eliminated those harrowing experiences.

Patient story

Bone Marrow Transplant for Sickle Cell Disease: Dallas’ Story

Sickle cell disease brings constant fear of life-threatening complications. A successful bone marrow transplant ended those fears for Dallas and her family.

Patient story

Bone Marrow Transplant to Treat Hurler Syndrome: Josie’s Story

18-month-old Josie received a stem cell transplant to stop a rare and devastating genetic condition in its tracks.

Patient story

Bone Marrow Transplant for Hurler Syndrome: Ethan’s Story

Diagnosed before his first birthday with a rare disease that causes ongoing damage to cells and organs, Ethan quickly received the only treatment that prevents further disease.

Patient story

Beta Thalassemia Major: Mia’s Story

From the time she was just a few months old, Mia needed blood transfusions due to her rare blood disease. A bone marrow transplant changed everything.