Cell and Gene Therapy Collaborative
The Cell and Gene Therapy Collaborative aims to build on Children's Hospital of Philadelphia's longstanding position at the forefront of cell and gene therapy research, which has already led to game-changing success. The Collaborative is designed to significantly increase the volume of new pediatric cell and gene therapy research and to accelerate the pace of clinical development by coordinating the efforts of multiple groups operating across the institution.
Cell and Gene Therapies for Children
There are currently three FDA-approved cell and gene therapies available for use in children in the United States. Two of them were developed by experts at Children's Hospital of Philadelphia.
Acute Lymphoblastic Leukemia
Spinal Muscular Atrophy
Innovation in the field of cell and gene therapy is moving at an incredible pace at CHOP. There are currently more than 20 clinical trials enrolling patients, with many more on the horizon.