Cell Therapy and Transplant Patient Stories
1 - 10 of 27
Leo Fought Like a Lion to Beat Stage 5 Kidney Cancer
Two hospitals work together to care for a 3-year-old with cancer and his family.
Gene Therapy for Sickle Cell Disease: Marie-Chantal’s Story
An FDA-approved gene therapy is giving people with sickle cell disease a future they didn’t think they’d have.
Experimental Gene Therapy for Hemophilia B: Bill’s Story
Bill’s hemophilia caused several serious health crises. After nearly 60 years of continual treatments, a gene therapy transformed his life.
Experimental Gene Therapy for Hemophilia B: Jay’s Story
For 50-plus years, Jay dealt with the frequent treatments needed for his hemophilia. A gene therapy put an end to the treatments and to the worry the disease caused him.
Experimental Gene Therapy for Hemophilia B: Bill’s Story
For nearly 50 years, Bill needed frequent treatment for hemophilia — often every few days. A gene therapy changed everything.
Acute Lymphoblastic Leukemia and CAR T-Cell Therapy: Asa’s Story
Diagnosed with leukemia at 3 months old, Asa received a revolutionary therapy that was pioneered at CHOP.
X-linked Lymphoproliferative Disease 1: Rafi’s Story
Genetic sequencing revealed that Rafi had an extremely rare, often fatal disease — and the discovery was amazingly made before he had serious symptoms.
CAR T-Cell Therapy for Relapsed ALL: Johnny’s Story
After multiple rounds of chemotherapy couldn’t wipe out Johnny’s cancer, he came to CHOP and received two versions of CAR T-cell therapy.
CAR T-Cell Therapy for Relapsed ALL: Daniel’s Story
Daniel’s leukemia came back five times. Since receiving an experimental treatment at CHOP called CAR T-cell therapy, he’s been cancer-free.
Bone Marrow Transplant to Treat Hurler Syndrome: Josie’s Story
18-month-old Josie received a stem cell transplant to stop a rare and devastating genetic condition in its tracks.