Cellular Therapy and Transplant Section Patients Stories Listing

Your child will be cared for by one of the most accomplished teams of cellular therapy and transplant experts in the world. Our team includes doctors, nurses, social workers, nutritionists, psychologists and more.

How we serve you

Existing patients or family members

215-590-3025

New patients, referrals and second opinions

267-426-0762

Patient story

Leo Fought Like a Lion to Beat Stage 5 Kidney Cancer

Two hospitals work together to care for a 3-year-old with cancer and his family.

Patient story

Gene Therapy for Sickle Cell Disease: Marie-Chantal’s Story

An FDA-approved gene therapy is giving people with sickle cell disease a future they didn’t think they’d have.

Patient story

Experimental Gene Therapy for Hemophilia B: Bill’s Story

Bill’s hemophilia caused several serious health crises. After nearly 60 years of continual treatments, a gene therapy transformed his life.

Patient story

Experimental Gene Therapy for Hemophilia B: Jay’s Story

For 50-plus years, Jay dealt with the frequent treatments needed for his hemophilia. A gene therapy put an end to the treatments and to the worry the disease caused him.

Patient story

Experimental Gene Therapy for Hemophilia B: Bill’s Story

For nearly 50 years, Bill needed frequent treatment for hemophilia — often every few days. A gene therapy changed everything.

Patient story

Acute Lymphoblastic Leukemia and CAR T-Cell Therapy: Asa’s Story

Diagnosed with leukemia at 3 months old, Asa received a revolutionary therapy that was pioneered at CHOP.

Patient story

X-linked Lymphoproliferative Disease 1: Rafi’s Story

Genetic sequencing revealed that Rafi had an extremely rare, often fatal disease — and the discovery was amazingly made before he had serious symptoms.