Gene Therapy in Hemophilia
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MitoAction
MitoAction’s mission is to improve the quality of life for children, adults, and families living with mitochondrial disease through support, education, outreach, advocacy and clinical research initiatives.
PALS (People Against Leigh Syndrome)
People Against Leigh Syndrome, (PALS), was formed in 2013 after William Martin, son of Neil and Lori Martin, was diagnosed with Leigh syndrome, a genetic neurometabolic disorder that can cause deterioration of the central nervous system, including the brain, spinal cord, and optic nerve.
The CHAMP Foundation
The Champ Foundation supports research toward better treatment and a cure for single large-scale mitochondrial deletion syndromes (SLSMDS), like Pearson syndrome.
Leigh Syndrome Parent Network: Facebook Support Group
This page is dedicated solely to the parents of children who have been diagnosed with Leigh's Syndrome - a mitochondrial disease.
International Mito Patients (IMP)
International Mito Patients is a network of national patient organizations involved in mito. The national patient organizations support and advocate for patients, fund research, increase awareness and improve education in their country.
The Lily Foundation
The Lily Foundation is the UK's leading mitochondrial disease charity and the largest charitable funder of mitochondrial research in Europe.
CureARS
CureARS Nonprofit is funding research for mt-aars disorders, mitochondrial ARS genes & providing support to families affected by the Mito ARS genes.
Leber’s Hereditary Optic Neuropathy (LHON)
This site was created by a family affected by Leber’s Hereditary Optic Neuropathy (LHON). By sharing what we learned as we struggled to cope with LHON, and what we've learned over the years since it first happened, we hope to help make the adjustment process smoother for others.
Mitochondrial Medicine Society (MMS)
Founded in 1998 by doctors Richard Haas and Robert Naviaux, the MMS represents an international group of physicians, researchers and clinicians working towards advancing education, research and global collaboration in clinical mitochondrial medicine.