CHOP Gene Therapy Experts Profiled in Philadelphia Magazine
Published on in CHOP News
CHOP researchers were interviewed as a part of a comprehensive article about cell and gene therapy in Philadelphia Magazine.
Hemophilia and Bleeding Disorders Program News and Updates
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CHOP-led Research Study Identifies Key Target in Treatment-Resistant Hemophilia A
Published on in CHOP News
CHOP researchers have identified BAFF as a key target that may be responsible for treatment failure in about 30% of patients with hemophilia A.
Researchers Uncover A Previously Underappreciated Mechanism that Turns Off Clotting Factor in Hemophilia A
Published on in CHOP News
CHOP researchers identified an in vivo role for activated protein C (APC), which could potentially be exploited for future hemophilia A treatments.
CHOP Volunteers Make Camp Special
Published on in Community Impact Report
CHOP volunteers make camp a reality for many kids with special medical needs. They not only keep them healthy, but they also take part of the activities and enjoy seeing kids being kids.
Gene-based Clotting Factor Prevents Bleeding in Animals with Hemophilia
Published on in CHOP News
A laboratory study may set the stage for a new preventive treatment for hemophilia patients who now develop antibodies to the standard treatment and then require a bypass therapy.
CHOP Investigator and Experimental One-dose Gene Therapy for Hemophilia B Featured in The New York Times
Published on in CHOP News
CHOP breakthrough helps scientists edge closer to defeating a longtime enemy of human health: hemophilia, the inability to form blood clots.
One-dose Gene Therapy Produces Clotting Factor, Safely Stops Bleeding in Hemophilia B Patients
Published on in CHOP News
A team of gene therapy researchers has reported on a highly active gene variant that achieved sustained factor levels in 10 adults, with no adverse effects.
Washington Post Reports on Hemophilia B Gene Therapy Advance
Published on in CHOP News
A clinical trial of a gene therapy for hemophilia B is allowing patients to avoid painful, disabling internal bleeds.
3 CHOP Scientists Win Bayer Grants for Hemophilia Research
Published on in CHOP News
Three CHOP researchers recently won grants for their work on hemophilia from the Bayer Hemophilia Awards Program.
After One Dose of Gene Therapy Hemophilia B Patients Maintain Near-normal Levels of Clotting Factor
Published on in CHOP News, International Update
In a clinical trial led by a CHOP researcher, adult patients with hemophilia B were able to pursue daily activities without disabling bleeds.